Avalglucosidase alfa

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Avalglucosidase alfa

Avalglucosidase alfa (pronunciation: av-al-gloo-KOH-si-dase AL-fa) is a enzyme replacement therapy used for the treatment of Pompe disease, a rare genetic disorder.

Etymology

The name "Avalglucosidase alfa" is derived from the enzyme it replaces, alpha-glucosidase. "Aval" is a prefix used in pharmaceutical naming to denote a modified version of a naturally occurring substance, in this case, the enzyme alpha-glucosidase. "Alfa" is a common suffix used in pharmaceutical naming to denote a product of recombinant DNA technology.

Usage

Avalglucosidase alfa is used to treat Pompe disease, a rare genetic disorder characterized by muscle weakness and respiratory problems. It works by replacing the enzyme alpha-glucosidase, which is deficient in people with Pompe disease.

Related Terms

  • Enzyme replacement therapy: A treatment method that involves replacing a missing or deficient enzyme in the body.
  • Pompe disease: A rare genetic disorder characterized by muscle weakness and respiratory problems.
  • Alpha-glucosidase: An enzyme that breaks down glycogen, a form of sugar stored in the body's cells.

See Also

External links

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