Pantothenate kinase-associated neurodegeneration

From WikiMD.org
Jump to navigation Jump to search

Pantothenate Kinase-Associated Neurodegeneration (PAN-doh-then-ate KIN-ase as-SO-see-ated NEU-ro-de-gen-er-ation) is a rare, genetic neurological disorder characterized by the progressive degeneration of the nervous system.

Etymology

The term "Pantothenate Kinase-Associated Neurodegeneration" is derived from the name of the enzyme Pantothenate Kinase that is affected in this disorder, and Neurodegeneration, which refers to the progressive loss of nerve cells.

Definition

Pantothenate Kinase-Associated Neurodegeneration (PKAN) is a type of Neurodegeneration with Brain Iron Accumulation (NBIA), a group of inherited neurological disorders in which iron accumulates in the basal ganglia causing progressive dystonia, spasticity, and other neurological symptoms. PKAN is caused by mutations in the PANK2 gene.

Symptoms

The symptoms of PKAN usually begin in early childhood and may include Dystonia (involuntary muscle contractions), Dysarthria (difficulty speaking), Parkinsonism (symptoms similar to Parkinson's disease), and Retinitis Pigmentosa (a group of rare genetic disorders that involve a breakdown and loss of cells in the retina).

Diagnosis

Diagnosis of PKAN is based on clinical examination, the presence of specific neurological symptoms, and confirmed by genetic testing showing mutations in the PANK2 gene.

Treatment

There is currently no cure for PKAN. Treatment is symptomatic and supportive, and may include physical therapy, medication for dystonia, and nutritional support due to difficulties with swallowing.

See Also

External links

Esculaap.svg

This WikiMD article is a stub. You can help make it a full article.


Languages: - East Asian 中文, 日本, 한국어, South Asian हिन्दी, Urdu, বাংলা, తెలుగు, தமிழ், ಕನ್ನಡ,
Southeast Asian Indonesian, Vietnamese, Thai, မြန်မာဘာသာ, European español, Deutsch, français, русский, português do Brasil, Italian, polski